Applied Therapeutics, Inc. announced promising 18 and 24-month results from the INSPIRE Phase 2/3 trial of govorestat, a treatment for Charcot-Marie-Tooth Sorbitol Dehydrogenase Deficiency (CMT-SORD).

Results from the ESTABLISH 1 observational study confirms that neuromuscular junction (NMJ) dysfunction is an underappreciated disease characteristic in patients with Charcot-Marie-Tooth disease (CMT) ...

The MarketWatch News Department was not involved in the creation of this content. Pat Livney's Personal Fight Sparks Immediate Action to Help Patients Walk Today and Invest in a Cure for Tomorrow ...

Improvements in outcomes and reduction in sorbitol maintained through 24 months Statistically significant correlation between absolute reduction in sorbitol and change in 10MWRT and CMT-FOM Lower Limb ...

9-1-1: Nashville star Isabelle Tate’s death is bringing attention to a rare disease. On Thursday, October 23, news broke that the actress had died at the age of 23. Her agency confirmed the news via ...

A magnifying glass. It indicates, "Click to perform a search". A magnifying glass. It indicates, "Click to perform a search". Interim Analysis from the Ongoing Open-Label Phase III Extension ...

CMT, we're on a mission to make an immediate impact on the lives of people living with CMT. Through strategic investments and ...

Country music star Alan Jackson has announced his farewell tour, “Last Call: One More for the Road,” and has promised to “give [fans] the best show I can,” Billboard reports. The Grammy-winning ...

The MarketWatch News Department was not involved in the creation of this content. Collaboration brings cutting-edge mobility support directly to the CMT community through strategic donation and ...

Alan Jackson revealed his Charcot-Marie-Tooth disease diagnosis on Tuesday (Sept. 28), and now he's hearing from fans who also battle CMT. Three things are clear about the singer's news, made in part ...